2024 Approvals

Alhemo A Breakthrough for Hemophilia Treatment

Alhemo A Breakthrough for Hemophilia Treatment

What is it prescribed for? Alhemo is used for routine prophylaxis to prevent or reduce the frequency of bleeding episodes in adults and children 12 years and older with hemophilia A (factor VIII deficiency) with inhibitors and hemophilia B (factor IX deficiency) with inhibitors. Alhemo was approved on December 2024. What is the name of the drug and what does it do?...

What to Know About ALYFTREK, A New Treatment For Cystic Fibrosis

What to Know About ALYFTREK, A New Treatment For Cystic Fibrosis

What is it prescribed for? ALYFTREK is prescribed for the treatment of cystic fibrosis (CF) in patients aged 6 years and older who have certain specific genetic mutations. This medication helps improve lung function and reduce symptoms of the disease. ALYFTREK was approved on December 20, 2024. What is the name of the drug and what does it do? The drug is called...

TRYNGOLZA: A New Treatment for Familial Chylomicronemia Syndrome (FCS)

TRYNGOLZA: A New Treatment for Familial Chylomicronemia Syndrome (FCS)

TRYNGOLZA is a new medication designed to help adults with familial chylomicronemia syndrome (FCS) manage their triglyceride levels. It is prescribed as an adjunct to a low-fat diet to reduce the risk of complications such as pancreatitis. TRYNGOLZA was approved on December 19, 2024. What is the name of the drug, and what does it do? TRYNGOLZA (pronounced...

ENSACOVE: A New Targeted Therapy for ALK-Positive Lung Cancer

ENSACOVE: A New Targeted Therapy for ALK-Positive Lung Cancer

ENSACOVE is a newly approved treatment for adults with anaplastic lymphoma kinase (ALK)-positive, locally advanced, or metastatic non-small cell lung cancer (NSCLC). It offers a new option for patients who have not previously received an ALK inhibitor. ENSACOVE was approved on December 18, 2024. What is the name of the drug, and what does it do? ENSACOVE (pronounced...

CRENESSITY: A New Treatment for Congenital Adrenal Hyperplasia (CAH)

CRENESSITY: A New Treatment for Congenital Adrenal Hyperplasia (CAH)

CRENESSITY offers a novel approach to managing classic congenital adrenal hyperplasia (CAH) in adults and children aged 4 years and older. This medication is designed to work alongside glucocorticoid replacement therapy to help control androgen levels and improve treatment outcomes. CRENESSITY was approved on December 13, 2024. What is the name of the drug, and what...

UNLOXCYT: A New Immunotherapy for Advanced Cutaneous Squamous Cell Carcinoma

UNLOXCYT: A New Immunotherapy for Advanced Cutaneous Squamous Cell Carcinoma

UNLOXCYT is an innovative immunotherapy offering hope for adults with metastatic or locally advanced cutaneous squamous cell carcinoma (CSCC) who are not candidates for surgery or radiation. This breakthrough treatment is designed to empower the immune system to target cancer more effectively. UNLOXCYT was approved on December 13, 2024. What is the name of the drug,...