VANRAFIA™ is prescribed for adults with a kidney disease called primary immunoglobulin A nephropathy (IgAN). This disease can damage the kidneys and lead to faster loss of kidney function. Doctors use VANRAFIA to lower the amount of protein in the urine (proteinuria), which is a sign of kidney damage. It was approved on April 2, 2025
What is it prescribed for? Alhemo is used for routine prophylaxis to prevent or reduce the frequency of bleeding episodes in adults and children 12 years and older with hemophilia A (factor VIII deficiency) with inhibitors and hemophilia B (factor IX deficiency) with inhibitors. Alhemo was approved on December 2024. What is the name of the drug and what does it do?...
What is it prescribed for? ALYFTREK is prescribed for the treatment of cystic fibrosis (CF) in patients aged 6 years and older who have certain specific genetic mutations. This medication helps improve lung function and reduce symptoms of the disease. ALYFTREK was approved on December 20, 2024. What is the name of the drug and what does it do? The drug is called...
TRYNGOLZA is a new medication designed to help adults with familial chylomicronemia syndrome (FCS) manage their triglyceride levels. It is prescribed as an adjunct to a low-fat diet to reduce the risk of complications such as pancreatitis. TRYNGOLZA was approved on December 19, 2024. What is the name of the drug, and what does it do? TRYNGOLZA (pronounced...
ENSACOVE is a newly approved treatment for adults with anaplastic lymphoma kinase (ALK)-positive, locally advanced, or metastatic non-small cell lung cancer (NSCLC). It offers a new option for patients who have not previously received an ALK inhibitor. ENSACOVE was approved on December 18, 2024. What is the name of the drug, and what does it do? ENSACOVE (pronounced...
CRENESSITY offers a novel approach to managing classic congenital adrenal hyperplasia (CAH) in adults and children aged 4 years and older. This medication is designed to work alongside glucocorticoid replacement therapy to help control androgen levels and improve treatment outcomes. CRENESSITY was approved on December 13, 2024. What is the name of the drug, and what...